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- Title
Transplantation using targeted busulfan for Diamond–Blackfan anemia.
- Authors
Kato, Shota; Nakano, Yoshiko; Hidaka, Moe; Sekiguchi, Masahiro; Watanabe, Kentaro; Fujimura, Junya; Kato, Motohiro
- Abstract
The article presents a case study of a three year old with Diamond–Blackfan anemia (DBA) who underwent allogeneic hematopoietic cell transplantation (HCT). It is reported that the patient received reduced-intensity conditioning with targeted busulfan. It is further reported that the patient achieved successful engraftment, became transfusion-independent, and showed no severe adverse events during the 12-month follow-up.
- Subjects
APLASTIC anemia treatment; GANCICLOVIR; HLA-B27 antigen; INTRAVENOUS therapy; BONE marrow transplantation; APLASTIC anemia; FERRITIN; TREATMENT effectiveness; BUSULFAN; HEMATOPOIETIC stem cell transplantation; RADIOTHERAPY; ROUTINE diagnostic tests
- Publication
Pediatrics International, 2023, Vol 65, Issue 1, p1
- ISSN
1328-8067
- Publication type
Case Study
- DOI
10.1111/ped.15440