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- Title
Treatment of adult storage disease: cost versus benefit.
- Authors
Buehler, B.
- Abstract
The article comments on the paper "Glycogen storage disease type II (Pompe disease): influence of enzyme replacement therapy in adults," by T. Merk and colleagues, in a 2008 issue. According to the author, the study should be the standard for the use of enzyme replacement in adults. He believes quality of life must be part of the data. He adds that the study emphasizes that treatment research must incorporate the human factor.
- Subjects
GLYCOGEN storage disease type II; THERAPEUTIC use of enzymes; GLYCOGEN storage disease; LYSOSOMAL storage diseases; MUSCULOSKELETAL system diseases
- Publication
European Journal of Neurology, 2009, Vol 16, Issue 2, p159
- ISSN
1351-5101
- Publication type
Editorial
- DOI
10.1111/j.1468-1331.2008.02374.x