Back to matchesWe found a matchYour institution may have access to this item. Find your institution then sign in to continue.TitleHealth outcomes in spinal muscular atrophy type 1 following AVXS‐101 gene replacement therapy.AuthorsAl‐Zaidy, Samiah; Pickard, A. Simon; Kotha, Kavitha; Alfano, Lindsay N.; Lowes, Linda; Paul, Grace; Church, Kathleen; Lehman, Kelly; Sproule, Douglas M.; Dabbous, Omar; Maru, Benit; Berry, Katherine; Arnold, W. David; Kissel, John T.; Mendell, Jerry R.; Shell, RichardPublicationPediatric Pulmonology, 2019, Vol 54, Issue 2, p179ISSN8755-6863Publication typeArticleDOI10.1002/ppul.24203